Knockdown of Muscle-Specific Ribosomal Protein L3-Like Enhances Muscle Function in Healthy and Dystrophic Mice
Kao, Betty R, Malerba, Alberto, Lu-Nguyen, Ngoc B, Harish, Pradeep, McCarthy, John J, Dickson, George, Popplewell, Linda J
Published in Nucleic acid therapeutics (01.12.2021)
Published in Nucleic acid therapeutics (01.12.2021)
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Combination Antisense Treatment for Destructive Exon Skipping of Myostatin and Open Reading Frame Rescue of Dystrophin in Neonatal mdx Mice
Lu-Nguyen, Ngoc B, Jarmin, Susan A, Saleh, Amer F, Popplewell, Linda, Gait, Michael J, Dickson, George
Published in Molecular therapy (01.08.2015)
Published in Molecular therapy (01.08.2015)
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Transgenic expression of human glial cell line-derived neurotrophic factor from integration-deficient lentiviral vectors is neuroprotective in a rodent model of Parkinson's disease
Lu-Nguyen, Ngoc B, Broadstock, Martin, Schliesser, Maximilian G, Bartholomae, Cynthia C, von Kalle, Christof, Schmidt, Manfred, Yáñez-Muñoz, Rafael J
Published in Human gene therapy (01.07.2014)
Published in Human gene therapy (01.07.2014)
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