Safety and Biological Efficacy of a Lipid–CFTR Complex for Gene Transfer in the Nasal Epithelium of Adult Patients with Cystic Fibrosis
Noone, Peadar G., Hohneker, Katherine W., Zhou, Zhaoqing, Johnson, Larry G., Foy, Carla, Gipson, Clay, Jones, Kim, Noah, Terry L., Leigh, Margaret W., Schwartzbach, Caryl, Efthimiou, John, Pearlman, Rodney, Boucher, Richard C., Knowles, Michael R.
Published in Molecular therapy (01.01.2000)
Published in Molecular therapy (01.01.2000)
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Journal Article
A double-blind, placebo controlled, dose ranging study to evaluate the safety and biological efficacy of the lipid-DNA complex GR213487B in the nasal epithelium of adult patients with cystic fibrosis
Knowles, M R, Noone, P G, Hohneker, K, Johnson, L G, Boucher, R C, Efthimiou, J, Crawford, C, Brown, R, Schwartzbach, C, Pearlman, R
Published in Human gene therapy (20.01.1998)
Published in Human gene therapy (20.01.1998)
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