Long-term Exon Skipping Studies With 2′-O-Methyl Phosphorothioate Antisense Oligonucleotides in Dystrophic Mouse Models
Tanganyika-de Winter, Christa L, Heemskerk, Hans, Karnaoukh, Tatyana G, van Putten, Maaike, de Kimpe, Sjef J, van Deutekom, Judith, Aartsma-Rus, Annemieke
Published in Molecular therapy. Nucleic acids (01.09.2012)
Published in Molecular therapy. Nucleic acids (01.09.2012)
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Learning, memory and blood–brain barrier pathology in Duchenne muscular dystrophy mice lacking Dp427, or Dp427 and Dp140
Verhaeg, Minou, Adamzek, Kevin, Vijver, Davy, Putker, Kayleigh, Engelbeen, Sarah, Wijnbergen, Daphne, Overzier, Maurice, Suidgeest, Ernst, Weerd, Louise, Aartsma‐Rus, Annemieke, Putten, Maaike
Published in Genes, brain and behavior (01.06.2024)
Published in Genes, brain and behavior (01.06.2024)
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Characterization of neuromuscular synapse function abnormalities in multiple Duchenne muscular dystrophy mouse models
van der Pijl, Elizabeth M., van Putten, Maaike, Niks, Erik H., Verschuuren, Jan J. G. M., Aartsma-Rus, Annemieke, Plomp, Jaap J.
Published in The European journal of neuroscience (01.06.2016)
Published in The European journal of neuroscience (01.06.2016)
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Nonclinical Exon Skipping Studies with 2′-O-Methyl Phosphorothioate Antisense Oligonucleotides in mdx and mdx-utrn−/− Mice Inspired by Clinical Trial Results
van Putten, Maaike, Tanganyika-de Winter, Christa, Bosgra, Sieto, Aartsma-Rus, Annemieke
Published in Nucleic acid therapeutics (01.04.2019)
Published in Nucleic acid therapeutics (01.04.2019)
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Assessment of Behavioral Characteristics With Procedures of Minimal Human Interference in the mdx Mouse Model for Duchenne Muscular Dystrophy
Engelbeen, Sarah, Aartsma-Rus, Annemieke, Koopmans, Bastijn, Loos, Maarten, van Putten, Maaike
Published in Frontiers in behavioral neuroscience (20.01.2021)
Published in Frontiers in behavioral neuroscience (20.01.2021)
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Differential myofiber-type transduction preference of adeno-associated virus serotypes 6 and 9
Riaz, Muhammad, Raz, Yotam, Moloney, Elizabeth B, van Putten, Maaike, Krom, Yvonne D, van der Maarel, Silvere M, Verhaagen, Joost, Raz, Vered
Published in Skeletal muscle (10.11.2015)
Published in Skeletal muscle (10.11.2015)
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Evaluation of 2’-Deoxy-2’-fluoro Antisense Oligonucleotides for Exon Skipping in Duchenne Muscular Dystrophy
Jirka, Silvana M G, Tanganyika-de Winter, Christa L, Boertje-van der Meulen, Joke W, van Putten, Maaike, Hiller, Monika, Vermue, Rick, de Visser, Peter C, Aartsma-Rus, Annemieke
Published in Molecular therapy. Nucleic acids (01.12.2015)
Published in Molecular therapy. Nucleic acids (01.12.2015)
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Preclinical Studies on Intestinal Administration of Antisense Oligonucleotides as a Model for Oral Delivery for Treatment of Duchenne Muscular Dystrophy
van Putten, Maaike, Young, Courtney, van den Berg, Sjoerd, Pronk, Amanda, Hulsker, Margriet, Karnaoukh, Tatyana G, Vermue, Rick, van Dijk, Ko Willems, de Kimpe, Sjef, Aartsma-Rus, Annemieke
Published in Molecular therapy. Nucleic acids (2014)
Published in Molecular therapy. Nucleic acids (2014)
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Challenges of Assessing Exon 53 Skipping of the Human DMD Transcript with Locked Nucleic Acid-Modified Antisense Oligonucleotides in a Mouse Model for Duchenne Muscular Dystrophy
Engelbeen, Sarah, O'Reilly, Daniel, Van De Vijver, Davy, Verhaart, Ingrid, van Putten, Maaike, Hariharan, Vignesh, Hassler, Matthew, Khvorova, Anastasia, Damha, Masad J, Aartsma-Rus, Annemieke
Published in Nucleic acid therapeutics (01.12.2023)
Published in Nucleic acid therapeutics (01.12.2023)
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Efficient Downregulation of Alk4 in Skeletal Muscle After Systemic Treatment with Conjugated siRNAs in a Mouse Model for Duchenne Muscular Dystrophy
Engelbeen, Sarah, Pasteuning-Vuhman, Svetlana, Boertje-van der Meulen, Joke, Parmar, Rubina, Charisse, Klaus, Sepp-Lorenzino, Laura, Manoharan, Muthiah, Aartsma-Rus, Annemieke, van Putten, Maaike
Published in Nucleic acid therapeutics (01.02.2023)
Published in Nucleic acid therapeutics (01.02.2023)
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