A novel Cas9 fusion protein promotes targeted genome editing with reduced mutational burden in primary human cells
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Published in Nucleic acids research (22.05.2023)
Published in Nucleic acids research (22.05.2023)
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Correction of IVS I-110(G>A) β-thalassemia by CRISPR/Cas-and TALEN-mediated disruption of aberrant regulatory elements in human hematopoietic stem and progenitor cells
Patsali, Petros, Turchiano, Giandomenico, Papasavva, Panayiota, Romito, Marianna, Loucari, Constantinos C, Stephanou, Coralea, Christou, Soteroulla, Sitarou, Maria, Mussolino, Claudio, Cornu, Tatjana I, Antoniou, Michael N, Lederer, Carsten W, Cathomen, Toni, Kleanthous, Marina
Published in Haematologica (Roma) (01.11.2019)
Published in Haematologica (Roma) (01.11.2019)
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Autonomous zinc-finger nuclease pairs for targeted chromosomal deletion
Söllü, Cem, Pars, Kaweh, Cornu, Tatjana I, Thibodeau-Beganny, Stacey, Maeder, Morgan L, Joung, J Keith, Heilbronn, Regine, Cathomen, Toni
Published in Nucleic acids research (01.12.2010)
Published in Nucleic acids research (01.12.2010)
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Designer epigenome modifiers enable robust and sustained gene silencing in clinically relevant human cells
Mlambo, Tafadzwa, Nitsch, Sandra, Hildenbeutel, Markus, Romito, Marianna, Müller, Maximilian, Bossen, Claudia, Diederichs, Sven, Cornu, Tatjana I, Cathomen, Toni, Mussolino, Claudio
Published in Nucleic acids research (18.05.2018)
Published in Nucleic acids research (18.05.2018)
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Function-Preserving Single Amino Acid Substitutions Shield Hematopoietic Stem and Progenitor Cells from CD117 Targeted Immunotherapy In Vivo
Marone, Romina, Lepore, Rosalba, Rositzka, Julia, Dettmer-Monaco, Viviane, dell' Aglio, Alessandro, Capoferri, Giuseppina, Brault, Julie, Ten Buren, Emiel, Burgold, Thomas, Camus, Anna, Divsalar, Christopher, Garcia Prat, Laura, Haydn, Anna, Hermann, Felix, Heugel, Marcel, Knezevic, Andreja, Lehmann, Frank Michael, Do Sacramento, Valentin, Sinopoli, Alessandro, Wellinger, Lisa C, Wiederkehr, Amélie, Yumlu, Saniye, Cathomen, Toni, Winkler, Thomas, Cornu, Tatjana I, Urlinger, Stefanie, Jeker, Lukas T
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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A Highly Efficient and GMP Compliant Protocol to Manufacture CCR5 Edited Cells to Treat HIV Infection
Romito, Marianna, Meyer, Emily, Poddar, Sushmita, Heinz, Helena, Rositzka, Julia, Hildenbeutel, Markus, Gautron, Anne-Sophie, Busser, Brian W, Kok, Yik Lim, Turchiano, Giandomenico, Haas, Simone, Schäfer, Richard, Smith, Julianne, Metzner, Karin J, Mussolino, Claudio, Duchateau, Philippe, Cathomen, Toni, Cornu, Tatjana I
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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