AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model
Evers, Melvin M., Miniarikova, Jana, Juhas, Stefan, Vallès, Astrid, Bohuslavova, Bozena, Juhasova, Jana, Skalnikova, Helena Kupcova, Vodicka, Petr, Valekova, Ivona, Brouwers, Cynthia, Blits, Bas, Lubelski, Jacek, Kovarova, Hana, Ellederova, Zdenka, van Deventer, Sander J., Petry, Harald, Motlik, Jan, Konstantinova, Pavlina
Published in Molecular therapy (05.09.2018)
Published in Molecular therapy (05.09.2018)
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A largely random AAV integration profile after LPLD gene therapy
Kaeppel, Christine, Beattie, Stuart G, Fronza, Raffaele, van Logtenstein, Richard, Salmon, Florence, Schmidt, Sabine, Wolf, Stephan, Nowrouzi, Ali, Glimm, Hanno, von Kalle, Christof, Petry, Harald, Gaudet, Daniel, Schmidt, Manfred
Published in Nature medicine (01.07.2013)
Published in Nature medicine (01.07.2013)
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Effect of Alipogene Tiparvovec (AAV1-LPLS447X) on Postprandial Chylomicron Metabolism in Lipoprotein Lipase-Deficient Patients
Carpentier, André C, Frisch, Frédérique, Labbé, Sébastien M, Gagnon, René, de Wal, Janneke, Greentree, Stephen, Petry, Harald, Twisk, Jaap, Brisson, Diane, Gaudet, Daniel
Published in The journal of clinical endocrinology and metabolism (01.05.2012)
Published in The journal of clinical endocrinology and metabolism (01.05.2012)
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Transient and intensive pharmacological immunosuppression fails to improve AAV-based liver gene transfer in non-human primates
Unzu, Carmen, Hervás-Stubbs, Sandra, Sampedro, Ana, Mauleón, Itsaso, Mancheño, Uxua, Alfaro, Carlos, de Salamanca, Rafael Enríquez, Benito, Alberto, Beattie, Stuart G, Petry, Harald, Prieto, Jesús, Melero, Ignacio, Fontanellas, Antonio
Published in Journal of translational medicine (15.06.2012)
Published in Journal of translational medicine (15.06.2012)
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Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5 ch and AAV1
Majowicz, Anna, Salas, David, Zabaleta, Nerea, Rodríguez-Garcia, Estefania, González-Aseguinolaza, Gloria, Petry, Harald, Ferreira, Valerie
Published in Molecular therapy (02.08.2017)
Published in Molecular therapy (02.08.2017)
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Sustained Enzymatic Correction by rAAV-Mediated Liver Gene Therapy Protects Against Induced Motor Neuropathy in Acute Porphyria Mice
Unzu, Carmen, Sampedro, Ana, Mauleón, Itsaso, Alegre, Manuel, Beattie, Stuart G, de Salamanca, Rafael Enríquez, Snapper, Jolanda, Twisk, Jaap, Petry, Harald, González-Aseguinolaza, Gloria, Artieda, Julio, Rodríguez-Pena, María Sol, Prieto, Jesús, Fontanellas, Antonio
Published in Molecular therapy (01.02.2011)
Published in Molecular therapy (01.02.2011)
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Long-term increased carnitine palmitoyltransferase 1A expression in ventromedial hypotalamus causes hyperphagia and alters the hypothalamic lipidomic profile
Mera, Paula, Mir, Joan Francesc, Fabriàs, Gemma, Casas, Josefina, Costa, Ana S H, Malandrino, Maria Ida, Fernández-López, José-Antonio, Remesar, Xavier, Gao, Su, Chohnan, Shigeru, Rodríguez-Peña, Maria Sol, Petry, Harald, Asins, Guillermina, Hegardt, Fausto G, Herrero, Laura, Serra, Dolors
Published in PloS one (12.05.2014)
Published in PloS one (12.05.2014)
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Optimization and comparison of knockdown efficacy between polymerase II expressed shRNA and artificial miRNA targeting luciferase and Apolipoprotein B100
Maczuga, Piotr, Koornneef, Annemart, Borel, Florie, Petry, Harald, van Deventer, Sander, Ritsema, Tita, Konstantinova, Pavlina
Published in BMC biotechnology (24.07.2012)
Published in BMC biotechnology (24.07.2012)
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Adeno-associated virus mediated delivery of Tregitope 167 ameliorates experimental colitis
van der Marel, Sander, Majowicz, Anna, Kwikkers, Karin, van Logtenstein, Richard, te Velde, Anje A, De Groot, Anne S, Meijer, Sybren L, van Deventer, Sander J, Petry, Harald, Hommes, Daniel W, Ferreira, Valerie
Published in World journal of gastroenterology : WJG (28.08.2012)
Published in World journal of gastroenterology : WJG (28.08.2012)
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Murine CD4⁺CD25⁻ cells activated in vitro with PMA/ionomycin and anti-CD3 acquire regulatory function and ameliorate experimental colitis in vivo
Majowicz, Anna, van der Marel, Sander, te Velde, Anje A, Meijer, Sybren L, Petry, Harald, van Deventer, Sander J, Ferreira, Valerie
Published in BMC gastroenterology (03.12.2012)
Published in BMC gastroenterology (03.12.2012)
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Molecular Cloning and Expression of Major Structural Protein VP1 of the Human Polyomavirus JC Virus: Formation of Virus-Like Particles Useful for Immunological and Therapeutic Studies
Goldmann, Claudia, Petry, Harald, Frye, Stephan, Ast, Oliver, Ebitsch, Susanne, Jentsch, Klaus-Dieter, Kaup, Franz-Josef, Weber, Frank, Trebst, Corinna, Nisslein, Thomas, Hunsmann, Gerhard, Weber, Thomas, Lüke, Wolfgang
Published in Journal of Virology (01.05.1999)
Published in Journal of Virology (01.05.1999)
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Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients
Gil-Farina, Irene, Fronza, Raffaele, Kaeppel, Christine, Lopez-Franco, Esperanza, Ferreira, Valerie, D'Avola, Delia, Benito, Alberto, Prieto, Jesus, Petry, Harald, Gonzalez-Aseguinolaza, Gloria, Schmidt, Manfred
Published in Molecular therapy (01.06.2016)
Published in Molecular therapy (01.06.2016)
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Naturally Occurring V1-env Region Variants Mediate Simian Immunodeficiency Virus SIVmac Escape from High-Titer Neutralizing Antibodies Induced by a Protective Subunit Vaccine
Petry, Harald, Pekrun, Katja, Hunsmann, Gerhard, Jurkiewicz, Elke, Lüke, Wolfgang
Published in Journal of Virology (01.12.2000)
Published in Journal of Virology (01.12.2000)
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424. AAV Re-Administration Following Pediatric Application: Effect of Age at First Administration
Pietersz, Kimberly L., vanDeventer, Sander J., Petry, Harald, Ferreira, Valerie
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5ch and AAV1
Majowicz, Anna, Salas, David, Zabaleta, Nerea, Rodríguez-Garcia, Estefania, González-Aseguinolaza, Gloria, Petry, Harald, Ferreira, Valerie
Published in Molecular therapy (02.08.2017)
Published in Molecular therapy (02.08.2017)
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