Optimization and comparison of knockdown efficacy between polymerase II expressed shRNA and artificial miRNA targeting luciferase and Apolipoprotein B100
Maczuga, Piotr, Koornneef, Annemart, Borel, Florie, Petry, Harald, van Deventer, Sander, Ritsema, Tita, Konstantinova, Pavlina
Published in BMC biotechnology (24.07.2012)
Published in BMC biotechnology (24.07.2012)
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Journal Article
Embedding siRNA sequences targeting Apolipoprotein B100 in shRNA and miRNA scaffolds results in differential processing and in vivo efficacy
Maczuga, Piotr, Lubelski, Jacek, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Fakkert, Erwin, Costessi, Adalberto, Butler, Derek, van Deventer, Sander, Petry, Harald, Koornneef, Annemart, Konstantinova, Pavlina
Published in Molecular therapy (01.01.2013)
Published in Molecular therapy (01.01.2013)
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Journal Article
Apolipoprotein B Knockdown by AAV-delivered shRNA Lowers Plasma Cholesterol in Mice
Koornneef, Annemart, Maczuga, Piotr, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Ritsema, Tita, van Deventer, Sander, Petry, Harald, Konstantinova, Pavlina
Published in Molecular therapy (01.04.2011)
Published in Molecular therapy (01.04.2011)
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Journal Article
Subunit-specific Incorporation Efficiency and Kinetics in Mitochondrial Complex I Homeostasis
Dieteren, Cindy E.J., Koopman, Werner J.H., Swarts, Herman G., Peters, Janny G.P., Maczuga, Piotr, van Gemst, Jasper J., Masereeuw, Rosalinde, Smeitink, Jan A.M., Nijtmans, Leo G.J., Willems, Peter H.G.M.
Published in The Journal of biological chemistry (07.12.2012)
Published in The Journal of biological chemistry (07.12.2012)
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Journal Article
Mir-142-3p target sequences reduce transgene directed immunogenicity following intramuscular AAV vector-mediated gene delivery
Anna, Majowicz, Piotr, Maczuga, Karin, Kwikkers, Sander, Van Der Marel, Richard, Van Logtenstein, Harald, Petry, Sander, Van Deventer, Pavlina, Konstantinova, Valerie, Ferreira
Published in Frontiers in immunology (2013)
Published in Frontiers in immunology (2013)
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Journal Article
In vivo knock-down of multidrug resistance transporters ABCC1 and ABCC2 by AAV-delivered shRNAs and by artificial miRNAs
Borel, Florie, van Logtenstein, Richard, Koornneef, Annemart, Maczuga, Piotr, Ritsema, Tita, Petry, Harald, van Deventer, Sander Jh, Jansen, Peter Lm, Konstantinova, Pavlina
Published in Journal of RNAi and gene silencing (2011)
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Published in Journal of RNAi and gene silencing (2011)
Journal Article